CSF and plasma concentrations of nusinersen | Download Scientific Diagram
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study - The Lancet
Mechanism of action of nusinersen | Download Scientific Diagram
Therapy development for spinal muscular atrophy: perspectives for muscular dystrophies and neurodegenerative disorders | Neurological Research and Practice | Full Text
Discovery of a CNS penetrant small molecule SMN2 splicing modulator with improved tolerability for spinal muscular atrophy | Scientific Reports
Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA) | National Institute of Neurological Disorders and Stroke
IJMS | Free Full-Text | Development of the Method for Nusinersen and Its Metabolites Identification in the Serum Samples of Children Treated with Spinraza for Spinal Muscular Atrophy
SPINRAZA (nusinersen) injection, for intrathecal use
The light at the end of the tunnel gets vivid for spinal muscular atrophy - Dutta - 2020 - Journal of Neurochemistry - Wiley Online Library
Nusinersen in the Treatment of Spinal Muscular Atrophy | SpringerLink
Frontiers | History of development of the life-saving drug “Nusinersen” in spinal muscular atrophy